Central nervous system stem cell transplantation for children with neuronal ceroid lipofuscinosis.

Object Infantile and late-infantile neuronal ceroid lipofuscinoses are invariably fatal lysosomal storage diseases associated with defects in lysosomal enzyme palmitoyl-protein thioesterase 1 or tripeptidyl peptidase 1 activity.

http://www.citeulike.org/user/leonardcj/article/12286893